Suchergebnisse - "muscular dystrophy"

PubPharm (13.178)

31

Functional cardiac consequences of β-adrenergic stress-induced injury in the mdx mouse model of Duchenne muscular dystrophy

enthalten in: bioRxiv : the preprint server for biology | 2024

von Earl, C. | Javier, A. | Richards, A. | +3

32

Casimersen (AMONDYS 45™) : An Antisense Oligonucleotide for Duchenne Muscular Dystrophy

enthalten in: Biomedicines | 2024

von Assefa, M. | Gepfert, A. | Zaheer, M. | +2

33

At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions : A Multi-Site Tissue Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives

enthalten in: ClinicalTrials.gov | 2024

34

Validation of a novel western blot assay to monitor patterns and levels of alpha dystroglycan in skeletal muscle of patients with limb girdle muscular dystrophies

enthalten in: Journal of muscle research and cell motility | 2024

von Rajasingham, T. | Rodriguez, H. | Betz, A. | +2

35

Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) : Long-Term Observational Study of Translarna Safety and Effectiveness in Usual Care

enthalten in: ClinicalTrials.gov | 2024

36

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim : Wearable Technology to Evaluate Hyperglycemia and Heart Rate Variability in Duchenne Muscular Dystrophy

enthalten in: ClinicalTrials.gov | 2024

37

Respiratory comorbidities and treatments in Duchenne muscular dystrophy : impact on life expectancy and causes of death

enthalten in: Journal of neurology | 2024

von Wahlgren, L. | Kroksmark, A. | Lindblad, A. | +2

38

Computer-Aided Diagnosis of Duchenne Muscular Dystrophy Based on Texture Pattern Recognition on Ultrasound Images Using Unsupervised Clustering Algorithms and Deep Learning

enthalten in: Ultrasound in medicine & biology | 2024

von Liao, A. | Wang, C. | Wang, C. | +6

39

Assessment of Neurodevelopmental Needs in Duchenne Muscular Dystrophy : Assessment of Neurodevelopmental Needs in Duchenne Muscular Dystrophy

enthalten in: ClinicalTrials.gov | 2024

40

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy : A Phase 1/2, Open-Label, Dose Escalation Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Multiple Intravenous Doses of BMN 351 in Participants With Duchenne Muscular Dystrophy

enthalten in: ClinicalTrials.gov | 2024