Suchergebnisse - "muscular dystrophy"

PubPharm (13.178)

101

Our journey with François Gros

enthalten in: Comptes rendus biologies | 2024

von Butler-Browne, G. | Mouly, V.

102

Memories of Professor François Gros

enthalten in: Comptes rendus biologies | 2024

von Takeda, S.

103

Challenges and Considerations of Preclinical Development for iPSC-Based Myogenic Cell Therapy

enthalten in: Cells | 2024

von Sun, C. | Serra, C. | Kalicharan, B. | +2

104

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice : Journey: A Global, Multicenter, Longitudinal Study of the Natural History of Subjects With Limb Girdle Muscular Dystrophy (LGMD) Type 2E (LGMD2E/R4), Type 2D (LGMD2D/R3), Type 2C (LGMD2C/R5), and Type 2A (LGMD2A/R1)

enthalten in: ClinicalTrials.gov | 2024

105

The muscle regeneration marker FOXP3 is associated with muscle injury in Duchenne muscular dystrophy

enthalten in: Brain & development | 2024

von Yannin Hernández-de la Cruz, S. | Ordaz-Robles, T. | Antonio Villaldama-Soriano, M. | +9

106

Association of a novel dystrophin (DMD) genetic nonsense variant in a cat with X-linked muscular dystrophy with a mild clinical course

enthalten in: Journal of veterinary internal medicine | 2024

von Muto, H. | Yu, Y. | Chambers, J. | +4

107

TRAPPC11-CDG muscular dystrophy : Review of 54 cases including a novel patient

enthalten in: Molecular genetics and metabolism | 2024

von Corona-Rivera, J. | Martínez-Duncker, I. | Morava, E. | +9

108

Evaluation of Neuromuscular Diseases and Complaints by Quantitative Muscle MRI

enthalten in: Journal of clinical medicine | 2024

von Schlaffke, L. | Rehmann, R. | Güttsches, A. | +6

109

Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene Therapy (FOX) : A Phase 2 Study to Evaluate the Effect of EDG-5506 on Safety, Pharmacokinetics, and Biomarkers in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene Therapy

enthalten in: ClinicalTrials.gov | 2024

110

A Study to Evaluate RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy : A Phase II, Multicenter, Randomized, Placebo-Controlled, Double-Blind Study to Evaluate the Pharmacodynamics, Safety, Tolerability, Pharmacokinetics, and Efficacy of RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy

enthalten in: ClinicalTrials.gov | 2024