Weiter zum Inhalt
Toggle navigation
English
English
Favoritenliste (
0
)
(Voll)
Kontakt
Mein Konto
Abmeldung
Mein Konto
Suche
Erweiterte Suche
Suchverlauf
Struktursuche
Narrative Service
Drug Overviews
Info Guide
/vufind/Search/Results?lookfor=%22Thrasher%2C+Adrian+J.%22&type=Person&sort=year
/vufind/Search/Results?lookfor=%22Thrasher%2C+Adrian+J.%22&type=Person&sort=year
Search /vufind/Search2/Results?lookfor=%22Thrasher%2C+Adrian+J.%22&type=Person&sort=year
PubPharm (545)
1
Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease
enthalten in:
Human gene therapy
| 2024
von
Whittaker, T.
|
Moula, S.
|
Bahal, S.
| +7
Wird geladen...
2
CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells
enthalten in:
Human gene therapy
| 2024
von
Rai, R.
|
Steinberg, Z.
|
Romito, M.
| +7
Wird geladen...
3
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant
enthalten in:
Molecular therapy : the journal of the American Society of Gene Therapy
| 2024
von
Yeung, J.
|
Liao, A.
|
Shaw, M.
| +15
Wird geladen...
4
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia
enthalten in:
The Journal of allergy and clinical immunology
| 2024
von
Bahal, S.
|
Zinicola, M.
|
Moula, S.
| +16
Wird geladen...
5
Investigating adverse genomic and regulatory changes caused by replacement of the full-length CFTR cDNA using Cas9 and AAV
enthalten in:
Molecular therapy. Nucleic acids
| 2024
von
Vaidyanathan, S.
|
Kerschner, J.
|
Paranjapye, A.
| +7
Wird geladen...
6
AAV capsid bioengineering in primary human retina models
enthalten in:
Scientific reports
| 2023
von
Westhaus, A.
|
Eamegdool, S.
|
Fernando, M.
| +15
Wird geladen...
7
CRISPR/Cas9-based disease modelling and functional correction of Interleukin 7 Receptor alpha Severe Combined Immunodeficiency in T-lymphocytes and hematopoietic stem cells
enthalten in:
bioRxiv.org
| 2023
von
Rai, R.
|
Steinberg, Z.
|
Romito, M.
| +7
Wird geladen...
8
An improved medium formulation for efficient ex vivo gene editing, expansion and engraftment of hematopoietic stem and progenitor cells
enthalten in:
Molecular therapy. Methods & clinical development
| 2023
von
Rai, R.
|
Naseem, A.
|
Vetharoy, W.
| +4
Wird geladen...
9
Assessment of Pre-Clinical Liver Models Based on Their Ability to Predict the Liver-Tropism of Adeno-Associated Virus Vectors
enthalten in:
Human gene therapy
| 2023
von
Westhaus, A.
|
Cabanes-Creus, M.
|
Dilworth, K.
| +24
ErratumIn: Hum Gene Ther. 2023 Jul;34(13-14):663. - PMID 37155618
Wird geladen...
10
Severe hematopoietic stem cell inflammation compromises chronic granulomatous disease gene therapy
enthalten in:
Cell reports. Medicine
| 2023
von
Sobrino, S.
|
Magnani, A.
|
Semeraro, M.
| +30
Wird geladen...
1
2
3
4
5
6
7
8
9
10
11
Nächster »
[55]
Filter & Sortierung
Treffer pro Seite
10
20
50
Sortieren
Relevanz
Neueste zuerst
Älteste zuerst
Verfasser
Zeitschriftentitel
Bibliothek
Standort (Printmedien)
Verwandte Substanzen
Verwandte Substanzen werden ermittelt...
Verwandte Erkrankungen/Symptome
Verwandte Erkrankungen/Symptome werden ermittelt...
Verwandte Gene
Verwandte Gene werden ermittelt...
Systematic Reviews
Clinical Studies
Patente
Covid-19/SARS-CoV-2
Exclude Systematic Reviews
Exclude Clinical Studies
Exclude Patents
Medienart
543
Aufsätze
299
E-Ressourcen
297
E-Artikel
246
Gedruckte Aufsätze
2
Bücher
2
E-Books
Alle anzeigen ...
weniger ...
Zeitschriftentitel
51
Blood
46
Molecular therapy
43
Molecular therapy : the journal of the American...
34
Human gene therapy
31
British journal of haematology
21
The Journal of allergy and clinical immunology
13
Molecular therapy. Methods & clinical development
11
Journal of clinical immunology
10
European journal of immunology
10
Scientific reports
9
Nature communications
9
Nature medicine
9
The journal of allergy and clinical immunology
8
The New England journal of medicine
7
Nature biotechnology
6
Blood cells, molecules, & diseases
6
Expert opinion on biological therapy
6
Journal of cell science
6
The Journal of experimental medicine
5
Current opinion in pharmacology
Alle anzeigen ...
weniger ...
Thema
287
Journal Article
229
Research Support, Non-U.S. Gov't
52
Review
52
Wiskott-Aldrich Syndrome Protein
35
Research Support, N.I.H., Extramural
23
gene therapy
21
Letter
20
Actins
18
Antigens, CD34
17
WAS protein, human
16
Adenosine Deaminase
16
EC 3.5.4.4
16
Was protein, mouse
15
Case Reports
14
NADPH Oxidases
13
EC 1.6.3.-
11
147336-22-9
11
Biomarkers
11
Klinische Studie
11
Cytokines
Alle anzeigen ...
weniger ...
Erscheinungszeitraum
55
2020-
286
2010-2019
167
2000-2009
Erscheinungsjahr(e)
Von:
Bis:
Sprache
390
Englisch
Haven't found what you're looking for?
Wird geladen...