Suchergebnisse - "Shieh, Perry B"

PubPharm (116)

71

Recruitment & retention program for the NeuroNEXT SMA Biomarker Study : Super Babies for SMA!

enthalten in: Contemporary clinical trials communications | 2018

von Bartlett, A. | Kolb, S. | Kingsley, A. | +25

ErratumIn: Contemp Clin Trials Commun. 2020 Dec 10;20:100688. - PMID 33392412

72

Congenital Myasthenic Syndromes

enthalten in: Neurologic clinics | 2018

von Shieh, P. | Oh, S.

73

A checklist for clinical trials in rare disease : obstacles and anticipatory actions-lessons learned from the FOR-DMD trial

enthalten in: Trials | 2018

von Crow, R. | Hart, K. | McDermott, M. | +45

74

A checklist for clinical trials in rare disease: obstacles and anticipatory actions—lessons learned from the FOR-DMD trial

enthalten in: Trials | 2018

von Crow, R. | Hart, K. | McDermott, M. | +45

75

A checklist for clinical trials in rare disease: obstacles and anticipatory actions—lessons learned from the FOR-DMD trial

enthalten in: Trials | 2018

von Crow, R. | Hart, K. | McDermott, M. | +45

76

Review of the Diagnosis and Treatment of Periodic Paralysis

enthalten in: Muscle & nerve | 2018

von Statland, J. | Fontaine, B. | Hanna, M. | +8

77

Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy

enthalten in: The New England journal of medicine | 2018

von Mercuri, E. | Darras, B. | Chiriboga, C. | +121

CommentIn: Nat Rev Neurol. 2018 Apr;14(4):196. - PMID 29497154

78

Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening

enthalten in: Journal of neuromuscular diseases | 2018

von Glascock, J. | Sampson, J. | Haidet-Phillips, A. | +12

CommentIn: Pediatr Neurol Briefs. 2019 Dec 31;33:5. - PMID 31929716

79

Natural history of infantile-onset spinal muscular atrophy

enthalten in: Annals of neurology | 2017

von Kolb, S. | Coffey, C. | Yankey, J. | +35

CommentIn: Ann Neurol. 2017 Dec;82(6):857-858. - PMID 29149769

80

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD) : a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

enthalten in: Lancet (London, England) | 2017

von McDonald, C. | Campbell, C. | Torricelli, R. | +72

CommentIn: Lancet. 2017 Sep 23;390(10101):1467-1468. - PMID 28728957