Suchergebnisse - "Shieh, Perry B"

PubPharm (8)

1

Real-World Outcomes in Patients with Spinal Muscular Atrophy Treated with Onasemnogene Abeparvovec Monotherapy : Findings from the RESTORE Registry

enthalten in: Journal of neuromuscular diseases | 2024

von Servais, L. | Day, J. | De Vivo, D. | +16

2

Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy : Phase I Ascending-Dose Study (STRONG)

enthalten in: Journal of neuromuscular diseases | 2023

von Finkel, R. | Darras, B. | Mendell, J. | +14

3

Experience and Perspectives in the US on the Evolving Treatment Landscape in Spinal Muscular Atrophy

enthalten in: International journal of general medicine | 2022

von Ramos-Platt, L. | Elman, L. | Shieh, P.

4

Safety and efficacy of nusinersen in spinal muscular atrophy : The EMBRACE study

enthalten in: Muscle & nerve | 2021

von Acsadi, G. | Crawford, T. | Müller-Felber, W. | +8

5

Incorporating Spinal Muscular Atrophy Analysis by Next-Generation Sequencing into a Comprehensive Multigene Panel for Neuromuscular Disorders

enthalten in: Genetic testing and molecular biomarkers | 2020

von Tan, C. | Westbrook, M. | Truty, R. | +4

6

Healthcare Utilization, Costs of Care, and Mortality Among Patients With Spinal Muscular Atrophy

enthalten in: Journal of health economics and outcomes research | 2019

von Tan, H. | Gu, T. | Chen, E. | +2

7

Healthcare Utilization, Costs of Care, and Mortality Among Psatients With Spinal Muscular Atrophy

enthalten in: Journal of health economics and outcomes research | 2019

von Tan, H. | Gu, T. | Chen, E. | +2

8

Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening

enthalten in: Journal of neuromuscular diseases | 2018

von Glascock, J. | Sampson, J. | Haidet-Phillips, A. | +12

CommentIn: Pediatr Neurol Briefs. 2019 Dec 31;33:5. - PMID 31929716

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