Suchergebnisse - "Shieh, Perry B"

PubPharm (7)

1

Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy : A Randomized Controlled Trial

enthalten in: Neurology | 2024

von Dang, U. | Damsker, J. | Guglieri, M. | +41

2

Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy : A Randomized Clinical Trial

enthalten in: JAMA neurology | 2022

von Guglieri, M. | Clemens, P. | Perlman, S. | +43

3

Quantitative Muscle Analysis in FSHD Using Whole-Body Fat-Referenced MRI : Composite Scores for Longitudinal and Cross-sectional Analysis

enthalten in: Neurology | 2022

von Mellion, M. | Widholm, P. | Karlsson, M. | +16

4

Genotype-phenotype correlations and novel molecular insights into the DHX30-associated neurodevelopmental disorders

enthalten in: Genome medicine | 2021

von Mannucci, I. | Dang, N. | Huber, H. | +62

5

Safety and efficacy of omaveloxolone in patients with mitochondrial myopathy : MOTOR trial

enthalten in: Neurology | 2020

von Madsen, K. | Buch, A. | Cohen, B. | +14

6

Natural history of infantile-onset spinal muscular atrophy

enthalten in: Annals of neurology | 2017

von Kolb, S. | Coffey, C. | Yankey, J. | +35

CommentIn: Ann Neurol. 2017 Dec;82(6):857-858. - PMID 29149769

7

Natural history of infantile‐onset spinal muscular atrophy

enthalten in: Annals of neurology | 2017

von Kolb, S. | Coffey, C. | Yankey, J. | +34

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