Suchergebnisse - "Shieh, Perry B"

PubPharm (3)

1

Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy

enthalten in: Neuromuscular disorders : NMD | 2021

von Campbell, C. | McColl, E. | McDermott, M. | +45

2

Disease-modifying effects of edasalonexent, an NF-κB inhibitor, in young boys with Duchenne muscular dystrophy : Results of the MoveDMD phase 2 and open label extension trial

enthalten in: Neuromuscular disorders : NMD | 2021

von Finkel, R. | Finanger, E. | Vandenborne, K. | +15

3

Large in-frame 5' deletions in DMD associated with mild Duchenne muscular dystrophy : Two case reports and a review of the literature

enthalten in: Neuromuscular disorders : NMD | 2019

von Gibbs, E. | Barthélémy, F. | Douine, E. | +6

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