Suchergebnisse - "Pipe, Steven W"

PubPharm (154)

1

Recommendations for a minimum data set for monitoring gene therapy in hemophilia : communication from the ISTH SSC Working Group on Gene Therapy

enthalten in: Journal of thrombosis and haemostasis : JTH | 2024

von Miesbach, W. | Konkle, B. | Chowdary, P. | +9

2

Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A

enthalten in: Journal of thrombosis and haemostasis : JTH | 2024

von Madan, B. | Ozelo, M. | Raheja, P. | +23

3

Emicizumab prophylaxis in infants with hemophilia A (HAVEN 7) : primary analysis of a phase 3b open-label trial

enthalten in: Blood | 2024

von Pipe, S. | Collins, P. | Dhalluin, C. | +15

CommentIn: Blood. 2024 Apr 4;143(14):1317-1318. - PMID 38573607

4

Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B) : 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial

enthalten in: The Lancet. Haematology | 2024

von Coppens, M. | Pipe, S. | Miesbach, W. | +36

5

Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants : Results from the phase III HOPE-B trial 2 years after gene therapy

enthalten in: Haemophilia : the official journal of the World Federation of Hemophilia | 2024

von Itzler, R. | Buckner, T. | Leebeek, F. | +5

6

Advancements in haemophilia A and health equity : is it time to redefine severity?

enthalten in: The Lancet. Haematology | 2024

von Weyand, A. | Malec, L. | Pipe, S.

7

Long-term outcomes with emicizumab in hemophilia A without inhibitors : results from the HAVEN 3 and 4 studies

enthalten in: Research and practice in thrombosis and haemostasis | 2024

von Mahlangu, J. | Jiménez-Yuste, V. | Ventriglia, G. | +11

8

Pharmacokinetics and coagulation biomarkers in children and adults with hemophilia A receiving emicizumab prophylaxis every 1, 2, or 4 weeks

enthalten in: Research and practice in thrombosis and haemostasis | 2024

von Kiialainen, A. | Adamkewicz, J. | Petry, C. | +11

9

Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1

enthalten in: Journal of thrombosis and haemostasis : JTH | 2023

von O'Mahony, B. | Dunn, A. | Leavitt, A. | +23

10

Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy

enthalten in: Blood advances | 2023

von von Drygalski, A. | Gomez, E. | Giermasz, A. | +11

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