Suchergebnisse - "Piechnik, Matthew"

PubPharm (4)

1

Sex Difference Leads to Differential Gene Expression Patterns and Therapeutic Efficacy in Mucopolysaccharidosis IVA Murine Model Receiving AAV8 Gene Therapy

enthalten in: International journal of molecular sciences | 2022

von Piechnik, M. | Amendum, P. | Sawamoto, K. | +9

2

Evading the AAV Immune Response in Mucopolysaccharidoses

enthalten in: International journal of molecular sciences | 2020

von Piechnik, M. | Sawamoto, K. | Ohnishi, H. | +3

3

Mucopolysaccharidosis IVA : Diagnosis, Treatment, and Management

enthalten in: International journal of molecular sciences | 2020

von Sawamoto, K. | Álvarez González, J. | Piechnik, M. | +4

4

Effect of enzyme replacement therapy on the growth of patients with Morquio A

enthalten in: Journal of human genetics | 2019

von Doherty, C. | Stapleton, M. | Piechnik, M. | +6

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