Suchergebnisse - "Muscular Atrophy"

PubPharm (6.330)

21

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy : Phase 2 Active Treatment Study to Evaluate the Efficacy and Safety of SRK-015 in Patients With Later-Onset Spinal Muscular Atrophy (TOPAZ)

enthalten in: ClinicalTrials.gov | 2024

22

High-intensity Interval Training in Patients With Spinal Muscular Atrophy : High-intensity Interval Training in Patients With Spinal Muscular Atrophy

enthalten in: ClinicalTrials.gov | 2024

23

Stasimon/Tmem41b is required for cell proliferation and adult mouse survival

enthalten in: Biochemical and biophysical research communications | 2024

von Carlini, M. | Van Alstyne, M. | Yang, H. | +3

24

A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of BIIB115 : A Randomized, Blinded, Placebo-Controlled, Phase 1 Single Ascending Dose Study in Healthy Adult Male Volunteers and an Open-Label Multiple Ascending Dose Study in Pediatric SMA Participants Previously Treated With Onasemnogene Abeparvovec (Zolgensma™) to Evaluate the Safety, Tolerability, and Pharmacokinetics of BIIB115

enthalten in: ClinicalTrials.gov | 2024

25

A Placebo-controlled Study of Clenbuterol in Spinal and Bulbar Muscular Atrophy : A Placebo-controlled Study to Evaluate the Efficacy and Safety of Clenbuterol in Patients With Spinal and Bulbar Muscular Atrophy (SBMA)

enthalten in: ClinicalTrials.gov | 2024

26

Recent research on home rehabilitation and nursing for spinal muscular atrophy

enthalten in: Zhongguo dang dai er ke za zhi = Chinese journal of contemporary pediatrics | 2024

von Leng, M. | Peng, H. | Wu, Z.

27

Risdiplam improves subjective swallowing quality in non-ambulatory adult patients with 5q-spinal muscular atrophy despite advanced motor impairment

enthalten in: Journal of neurology | 2024

von Brakemeier, S. | Lipka, J. | Schlag, M. | +2

28

Metabolomics of cerebrospinal fluid reveals candidate diagnostic biomarkers to distinguish between spinal muscular atrophy type II and type III

enthalten in: CNS neuroscience & therapeutics | 2024

von Lu, M. | Wang, X. | Sun, N. | +3

29

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab-ONYX : An Open-Label, Multicenter, Extension Trial to Evaluate the Long-Term Safety and Efficacy of Apitegromab in Patients With Type 2 and Type 3 Spinal Muscular Atrophy Who Completed Previous Investigational Trials of Apitegromab

enthalten in: ClinicalTrials.gov | 2024

30

A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy : A Phase II, Open-label Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy

enthalten in: ClinicalTrials.gov | 2024