Suchergebnisse - "Mouly, Vincent"

PubPharm (15)

1

Cell-mediated exon skipping normalizes dystrophin expression and muscle function in a new mouse model of Duchenne Muscular Dystrophy

enthalten in: EMBO molecular medicine | 2024

von Galli, F. | Bragg, L. | Rossi, M. | +16

2

Immortalized Canine Dystrophic Myoblast Cell Lines for Development of Peptide-Conjugated Splice-Switching Oligonucleotides

enthalten in: Nucleic acid therapeutics | 2021

von Tone, Y. | Mamchaoui, K. | Tsoumpra, M. | +12

3

Exons 45-55 Skipping Using Mutation-Tailored Cocktails of Antisense Morpholinos in the DMD Gene

enthalten in: Molecular therapy : the journal of the American Society of Gene Therapy | 2019

von Echigoya, Y. | Lim, K. | Melo, D. | +11

4

Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next-generation human artificial chromosomes for Duchenne muscular dystrophy

enthalten in: EMBO molecular medicine | 2018

von Benedetti, S. | Uno, N. | Hoshiya, H. | +18

5

Flow Cytometry-Defined CD49d Expression in Circulating T-Lymphocytes Is a Biomarker for Disease Progression in Duchenne Muscular Dystrophy

enthalten in: Methods in molecular biology (Clifton, N.J.) | 2018

von Savino, W. | Pinto-Mariz, F. | Mouly, V.

6

Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy

enthalten in: Molecular therapy : the journal of the American Society of Gene Therapy | 2017

von Echigoya, Y. | Lim, K. | Trieu, N. | +15

7

Selection-free gene repair after adenoviral vector transduction of designer nucleases : rescue of dystrophin synthesis in DMD muscle cell populations

enthalten in: Nucleic acids research | 2016

von Maggio, I. | Stefanucci, L. | Janssen, J. | +4

8

FUBP1 : a new protagonist in splicing regulation of the DMD gene

enthalten in: Nucleic acids research | 2015

von Miro, J. | Laaref, A. | Rofidal, V. | +8

9

In silico screening based on predictive algorithms as a design tool for exon skipping oligonucleotides in Duchenne muscular dystrophy

enthalten in: PloS one | 2015

von Echigoya, Y. | Mouly, V. | Garcia, L. | +2

10

Predictive markers of clinical outcome in the GRMD dog model of Duchenne muscular dystrophy

enthalten in: Disease models & mechanisms | 2014

von Barthélémy, I. | Pinto-Mariz, F. | Yada, E. | +8

CommentIn: Dis Model Mech. 2015 Mar;8(3):193-4. - PMID 25740329