Suchergebnisse - "Miesbach, Wolfgang"

PubPharm (9)

1

Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B) : 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial

enthalten in: The Lancet. Haematology | 2024

von Coppens, M. | Pipe, S. | Miesbach, W. | +36

2

The current challenges faced by people with hemophilia B

enthalten in: European journal of haematology | 2024

von Miesbach, W. | von Drygalski, A. | Smith, C. | +5

3

Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy

enthalten in: Blood advances | 2023

von von Drygalski, A. | Gomez, E. | Giermasz, A. | +11

4

Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B

enthalten in: The New England journal of medicine | 2023

von Pipe, S. | Leebeek, F. | Recht, M. | +35

CommentIn: N Engl J Med. 2023 May 18;388(20):1918. - PMID 37195960

5

Gene therapy for hemophilia : a review on clinical benefit, limitations, and remaining issues

enthalten in: Blood | 2021

von Leebeek, F. | Miesbach, W.

6

Practical Implications of Factor IX Gene Transfer for Individuals with Hemophilia B : A Clinical Perspective

enthalten in: Human gene therapy. Clinical development | 2018

von Miesbach, W. | Sawyer, E.

7

Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B

enthalten in: Blood | 2018

von Miesbach, W. | Meijer, K. | Coppens, M. | +11

CommentIn: Blood. 2018 Mar 1;131(9):952-953. - PMID 29496703

8

Engineered factor IX variants bypass FVIII and correct hemophilia A phenotype in mice

enthalten in: Blood | 2012

von Milanov, P. | Ivanciu, L. | Abriss, D. | +7

CommentIn: Blood. 2012 Jan 12;119(2):325-6. - PMID 22247519

9

Comprehensive treatment of periodontitis in patients with von Willebrand disease

enthalten in: Journal of periodontology | 2010

von Nickles, K. | Wohlfeil, M. | Alesci, S. | +2

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