Suchergebnisse - "Mendonca, Rodrigo"

PubPharm (3)

1

Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2) : secondary analyses from an open-label trial

enthalten in: The Lancet. Neurology | 2022

von Masson, R. | Mazurkiewicz-Bełdzińska, M. | Rose, K. | +120

CommentIn: Lancet Neurol. 2022 Dec;21(12):1065-1066. - PMID 36244363

2

Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls

enthalten in: The New England journal of medicine | 2021

von Darras, B. | Masson, R. | Mazurkiewicz-Bełdzińska, M. | +116

3

Risdiplam in Type 1 Spinal Muscular Atrophy

enthalten in: The New England journal of medicine | 2021

von Baranello, G. | Darras, B. | Day, J. | +115

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