Suchergebnisse - "McDonald, Craig M"

PubPharm (280)

41

Clinical and Genetic Characteristics in Young, Glucocorticoid-Naive Boys With Duchenne Muscular Dystrophy

enthalten in: Neurology | 2022

von Schiava, M. | Amos, R. | VanRuiten, H. | +48

42

Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD) : Observations from a phase 2 trial

enthalten in: PloS one | 2022

von Muntoni, F. | Guglieri, M. | Mah, J. | +9

43

A Combined Prospective and Retrospective Comparison of Long-Term Functional Outcomes Suggests Delayed Loss of Ambulation and Pulmonary Decline with Long-Term Eteplirsen Treatment

enthalten in: Journal of neuromuscular diseases | 2022

von Mitelman, O. | Abdel-Hamid, H. | Byrne, B. | +15

44

Comparing Deflazacort and Prednisone in Duchenne Muscular Dystrophy

enthalten in: Journal of neuromuscular diseases | 2022

von Biggar, W. | Skalsky, A. | McDonald, C.

45

Influence of β1 Adrenergic Receptor Genotype on Longitudinal Measures of Left Ventricular Ejection Fraction and Responsiveness to ß-Blocker Therapy in Patients With Duchenne Muscular Dystrophy

enthalten in: Clinical Medicine Insights. Cardiology | 2022

von Kelley, E. | Cross, T. | McDonald, C. | +4

46

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy : A 30-Month Nonrandomized Controlled Open-Label Extension Trial

enthalten in: JAMA network open | 2022

von Mah, J. | Clemens, P. | Guglieri, M. | +125

47

Long-Term Functional Efficacy and Safety of Viltolarsen in Patients with Duchenne Muscular Dystrophy

enthalten in: Journal of neuromuscular diseases | 2022

von Clemens, P. | Rao, V. | Connolly, A. | +8

48

Delays in pulmonary decline in eteplirsen‐treated patients with Duchenne muscular dystrophy

enthalten in: Muscle & Nerve | 2022

von Iff, J. | Gerrits, C. | Zhong, Y. | +6

49

Influence of β2 adrenergic receptor genotype on longitudinal measures of forced vital capacity in patients with Duchenne muscular dystrophy

enthalten in: Neuromuscular disorders : NMD | 2022

von Kelley, E. | Cross, T. | McDonald, C. | +2

50

Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy

enthalten in: Journal of comparative effectiveness research | 2021

von Shieh, P. | Elfring, G. | Trifillis, P. | +111