Suchergebnisse - "McDonald, Craig M"

PubPharm (18)

1

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy : Results From the Phase 2, Open-Label, 4-Year Extension Study

enthalten in: Journal of neuromuscular diseases | 2023

von Clemens, P. | Rao, V. | Connolly, A. | +8

2

Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy : A Randomized Clinical Trial

enthalten in: JAMA | 2022

von Guglieri, M. | Bushby, K. | McDermott, M. | +61

3

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy : A 30-Month Nonrandomized Controlled Open-Label Extension Trial

enthalten in: JAMA network open | 2022

von Mah, J. | Clemens, P. | Guglieri, M. | +125

4

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

enthalten in: PLoS medicine | 2020

von Smith, E. | Conklin, L. | Hoffman, E. | +24

5

Genetic modifiers of respiratory function in Duchenne muscular dystrophy

enthalten in: Annals of clinical and translational neurology | 2020

von Bello, L. | D'Angelo, G. | Villa, M. | +38

6

Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function

enthalten in: Neurology | 2019

von Hoffman, E. | Schwartz, B. | Mengle-Gaw, L. | +28

7

Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy

enthalten in: Muscle & nerve | 2019

von Connolly, A. | Zaidman, C. | Golumbek, P. | +16

CommentIn: Muscle Nerve. 2019 Jun;59(6):638-639. - PMID 30993732

8

Longitudinal pulmonary function testing outcome measures in Duchenne muscular dystrophy : Long-term natural history with and without glucocorticoids

enthalten in: Neuromuscular disorders : NMD | 2018

von McDonald, C. | Gordish-Dressman, H. | Henricson, E. | +45

9

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy : a prospective cohort study

enthalten in: Lancet (London, England) | 2018

von McDonald, C. | Henricson, E. | Abresch, R. | +44

CommentIn: Lancet. 2018 Feb 3;391(10119):406-407. - PMID 29174483

10

A phase 3 randomized placebo-controlled trial of tadalafil for Duchenne muscular dystrophy

enthalten in: Neurology | 2017

von Victor, R. | Sweeney, H. | Finkel, R. | +77