Suchergebnisse - "Markati, Theodora"

PubPharm (13)

1

The use of digital outcome measures in clinical trials in rare neurological diseases : a systematic literature review

enthalten in: Orphanet journal of rare diseases | 2023

von Poleur, M. | Markati, T. | Servais, L.

2

The use of digital outcome measures in clinical trials in rare neurological diseases: a systematic literature review

enthalten in: Orphanet journal of rare diseases | 2023

von Poleur, M. | Markati, T. | Servais, L.

3

The use of digital outcome measures in clinical trials in rare neurological diseases: a systematic literature review

enthalten in: Orphanet journal of rare diseases | 2023

von Poleur, M. | Markati, T. | Servais, L.

4

A systematic review of adeno-associated virus gene therapies in neurology : the need for consistent safety monitoring of a promising treatment

enthalten in: Journal of neurology, neurosurgery, and psychiatry | 2022

von Horton, R. | Saade, D. | Markati, T. | +4

5

Early clinical and pre-clinical therapy development in Nemaline myopathy

enthalten in: Expert opinion on therapeutic targets | 2022

von Fisher, G. | Mackels, L. | Markati, T. | +5

6

Emerging therapies for Duchenne muscular dystrophy

enthalten in: The Lancet. Neurology | 2022

von Markati, T. | Oskoui, M. | Farrar, M. | +3

7

Risdiplam : an investigational survival motor neuron 2 (SMN2) splicing modifier for spinal muscular atrophy (SMA)

enthalten in: Expert opinion on investigational drugs | 2022

von Markati, T. | Fisher, G. | Ramdas, S. | +1

8

Risdiplam: an investigational survival motor neuron 2 (SMN2) splicing modifier for spinal muscular atrophy (SMA)

enthalten in: Expert opinion on investigational drugs | 2022

von Markati, T. | Fisher, G. | Ramdas, S. | +1

9

Therapies in preclinical and clinical development for Angelman syndrome

enthalten in: Expert opinion on investigational drugs | 2021

von Markati, T. | Duis, J. | Servais, L.

10

Lessons Learned from Discontinued Clinical Developments in Duchenne Muscular Dystrophy

enthalten in: Frontiers in pharmacology | 2021

von Markati, T. | De Waele, L. | Schara-Schmidt, U. | +1