Suchergebnisse - "Mah, Jean K"

PubPharm (203)

21

Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD) : Observations from a phase 2 trial

enthalten in: PloS one | 2022

von Muntoni, F. | Guglieri, M. | Mah, J. | +9

22

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy : A 30-Month Nonrandomized Controlled Open-Label Extension Trial

enthalten in: JAMA network open | 2022

von Mah, J. | Clemens, P. | Guglieri, M. | +125

23

Long-Term Functional Efficacy and Safety of Viltolarsen in Patients with Duchenne Muscular Dystrophy

enthalten in: Journal of neuromuscular diseases | 2022

von Clemens, P. | Rao, V. | Connolly, A. | +8

24

Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy

enthalten in: Journal of comparative effectiveness research | 2021

von Shieh, P. | Elfring, G. | Trifillis, P. | +111

25

Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy

enthalten in: Neuromuscular disorders : NMD | 2021

von Campbell, C. | McColl, E. | McDermott, M. | +45

26

Longitudinally extensive transverse myelitis with positive aquaporin-4 IgG associated with dengue infection : a case report and systematic review of cases

enthalten in: Multiple sclerosis and related disorders | 2021

von Comtois, J. | Camara-Lemarroy, C. | Mah, J. | +5

27

Rasch Analysis of the Pediatric Quality of Life Inventory 4.0 Generic Core Scales Administered to Patients With Duchenne Muscular Dystrophy

enthalten in: Value in health : the journal of the International Society for Pharmacoeconomics and Outcomes Research | 2021

von Landfeldt, E. | Iff, J. | Henricson, E. | +37

28

Comparison of Spinal Cord Magnetic Resonance Imaging Features Among Children With Acquired Demyelinating Syndromes

enthalten in: JAMA network open | 2021

von Fadda, G. | Alves, C. | O'Mahony, J. | +35

29

Corneal Confocal Microscopy Predicts the Development of Diabetic Neuropathy : A Longitudinal Diagnostic Multinational Consortium Study

enthalten in: Diabetes care | 2021

von Perkins, B. | Lovblom, L. | Lewis, E. | +19

30

Correction to : Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study

enthalten in: Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics | 2021

von Rudnicki, S. | Andrews, J. | Duong, T. | +20

ErratumFor: Neurotherapeutics. 2021 Apr;18(2):1127-1136. - PMID 33624184