Suchergebnisse - "Mah, Jean K"

PubPharm (23)

1

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS) : a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

enthalten in: The Lancet. Neurology | 2024

von Mercuri, E. | Vilchez, J. | Boespflug-Tanguy, O. | +25

ErratumIn: Lancet Neurol. 2024 Apr 18;:. - PMID 38643778

2

Understanding the experiences of lung volume recruitment among boys with Duchenne muscular dystrophy : A multicenter qualitative study

enthalten in: Pediatric pulmonology | 2023

von Katz, S. | Blinder, H. | Newhook, D. | +10

3

Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy : A Randomized Clinical Trial

enthalten in: JAMA neurology | 2022

von Guglieri, M. | Clemens, P. | Perlman, S. | +43

4

Routine lung volume recruitment in boys with Duchenne muscular dystrophy : a randomised clinical trial

enthalten in: Thorax | 2022

von Katz, S. | Mah, J. | McMillan, H. | +16

CommentIn: Thorax. 2022 Aug;77(8):743-744. - PMID 35470244

5

Quantitative magnetic resonance imaging measures as biomarkers of disease progression in boys with Duchenne muscular dystrophy : a phase 2 trial of domagrozumab

enthalten in: Journal of neurology | 2022

von Sherlock, S. | Palmer, J. | Wagner, K. | +13

6

A National Spinal Muscular Atrophy Registry for Real-World Evidence

enthalten in: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques | 2020

von Hodgkinson, V. | Oskoui, M. | Lounsberry, J. | +47

7

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

enthalten in: PLoS medicine | 2020

von Smith, E. | Conklin, L. | Hoffman, E. | +24

8

Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping : A Phase 2 Randomized Clinical Trial

enthalten in: JAMA neurology | 2020

von Clemens, P. | Rao, V. | Connolly, A. | +11

ErratumIn: JAMA Neurol. 2020 Aug 1;77(8):1040. - PMID 32539096

9

Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug

enthalten in: Pharmacological research | 2018

von Conklin, L. | Damsker, J. | Hoffman, E. | +29

10

Corneal confocal microscopy for identification of diabetic sensorimotor polyneuropathy : a pooled multinational consortium study

enthalten in: Diabetologia | 2018

von Perkins, B. | Lovblom, L. | Bril, V. | +19