Suchergebnisse - "Mah, Jean K"

PubPharm (9)

1

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy : Results From the Phase 2, Open-Label, 4-Year Extension Study

enthalten in: Journal of neuromuscular diseases | 2023

von Clemens, P. | Rao, V. | Connolly, A. | +8

2

Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy : A Randomized Clinical Trial

enthalten in: JAMA | 2022

von Guglieri, M. | Bushby, K. | McDermott, M. | +61

3

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy : A 30-Month Nonrandomized Controlled Open-Label Extension Trial

enthalten in: JAMA network open | 2022

von Mah, J. | Clemens, P. | Guglieri, M. | +125

4

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

enthalten in: PLoS medicine | 2020

von Smith, E. | Conklin, L. | Hoffman, E. | +24

5

Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function

enthalten in: Neurology | 2019

von Hoffman, E. | Schwartz, B. | Mengle-Gaw, L. | +28

6

Disease-specific and glucocorticoid-responsive serum biomarkers for Duchenne Muscular Dystrophy

enthalten in: Scientific reports | 2019

von Hathout, Y. | Liang, C. | Ogundele, M. | +11

7

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy : a prospective cohort study

enthalten in: Lancet (London, England) | 2018

von McDonald, C. | Henricson, E. | Abresch, R. | +44

CommentIn: Lancet. 2018 Feb 3;391(10119):406-407. - PMID 29174483

8

The cooperative international neuromuscular research group Duchenne natural history study : glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures

enthalten in: Muscle & nerve | 2013

von Henricson, E. | Abresch, R. | Cnaan, A. | +110

9

The cooperative international neuromuscular research group Duchenne natural history study--a longitudinal investigation in the era of glucocorticoid therapy : design of protocol and the methods used

enthalten in: Muscle & nerve | 2013

von McDonald, C. | Henricson, E. | Abresch, R. | +109

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