Suchergebnisse - "Mah, Jean K"

PubPharm (9)

1

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy : Results From the Phase 2, Open-Label, 4-Year Extension Study

enthalten in: Journal of neuromuscular diseases | 2023

von Clemens, P. | Rao, V. | Connolly, A. | +8

2

Long-Term Functional Efficacy and Safety of Viltolarsen in Patients with Duchenne Muscular Dystrophy

enthalten in: Journal of neuromuscular diseases | 2022

von Clemens, P. | Rao, V. | Connolly, A. | +8

3

The CINRG Becker Natural History Study : Baseline characteristics

enthalten in: Muscle & nerve | 2020

von Clemens, P. | Niizawa, G. | Feng, J. | +24

4

Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping : A Phase 2 Randomized Clinical Trial

enthalten in: JAMA neurology | 2020

von Clemens, P. | Rao, V. | Connolly, A. | +11

ErratumIn: JAMA Neurol. 2020 Aug 1;77(8):1040. - PMID 32539096

5

An Overview of Recent Therapeutics Advances for Duchenne Muscular Dystrophy

enthalten in: Methods in molecular biology (Clifton, N.J.) | 2018

von Mah, J.

6

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD) : a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

enthalten in: Lancet (London, England) | 2017

von McDonald, C. | Campbell, C. | Torricelli, R. | +72

CommentIn: Lancet. 2017 Sep 23;390(10101):1467-1468. - PMID 28728957

7

Discovery of serum protein biomarkers in the mdx mouse model and cross-species comparison to Duchenne muscular dystrophy patients

enthalten in: Human molecular genetics | 2014

von Hathout, Y. | Marathi, R. | Rayavarapu, S. | +13

8

Ataluren treatment of patients with nonsense mutation dystrophinopathy

enthalten in: Muscle & nerve | 2014

von Bushby, K. | Finkel, R. | Wong, B. | +132

9

A population-based study of dystrophin mutations in Canada

enthalten in: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques | 2011

von Mah, J. | Selby, K. | Campbell, C. | +10

CommentIn: Can J Neurol Sci. 2011 May;38(3):387. - PMID 21515491

1
[1]