Suchergebnisse - "Mah, Jean K"

PubPharm (8)

1

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy : Results From the Phase 2, Open-Label, 4-Year Extension Study

enthalten in: Journal of neuromuscular diseases | 2023

von Clemens, P. | Rao, V. | Connolly, A. | +8

2

Quantitative magnetic resonance imaging measures as biomarkers of disease progression in boys with Duchenne muscular dystrophy : a phase 2 trial of domagrozumab

enthalten in: Journal of neurology | 2022

von Sherlock, S. | Palmer, J. | Wagner, K. | +13

3

Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD) : Observations from a phase 2 trial

enthalten in: PloS one | 2022

von Muntoni, F. | Guglieri, M. | Mah, J. | +9

4

Reldesemtiv in Patients with Spinal Muscular Atrophy : a Phase 2 Hypothesis-Generating Study

enthalten in: Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics | 2021

von Rudnicki, S. | Andrews, J. | Duong, T. | +20

ErratumIn: Neurotherapeutics. 2021 Jul;18(3):2130. - PMID 34731415

5

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

enthalten in: PLoS medicine | 2020

von Smith, E. | Conklin, L. | Hoffman, E. | +24

6

Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping : A Phase 2 Randomized Clinical Trial

enthalten in: JAMA neurology | 2020

von Clemens, P. | Rao, V. | Connolly, A. | +11

ErratumIn: JAMA Neurol. 2020 Aug 1;77(8):1040. - PMID 32539096

7

Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy

enthalten in: Neuromuscular disorders : NMD | 2020

von Wagner, K. | Abdel-Hamid, H. | Mah, J. | +21

ErratumIn: Neuromuscul Disord. 2021 Feb;31(2):167-168. - PMID 33451933

8

Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug

enthalten in: Pharmacological research | 2018

von Conklin, L. | Damsker, J. | Hoffman, E. | +29

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