Suchergebnisse - "Mah, Jean K"

PubPharm (169)

1

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS) : a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

enthalten in: The Lancet. Neurology | 2024

von Mercuri, E. | Vilchez, J. | Boespflug-Tanguy, O. | +25

ErratumIn: Lancet Neurol. 2024 Apr 18;:. - PMID 38643778

2

Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy : A Randomized Controlled Trial

enthalten in: Neurology | 2024

von Dang, U. | Damsker, J. | Guglieri, M. | +41

3

A Study on the Incidence and Prevalence of 5q Spinal Muscular Atrophy in Canada Using Multiple Data Sources

enthalten in: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques | 2024

von Price, T. | Hodgkinson, V. | Westbury, G. | +7

4

Alberta Spinal Muscular Atrophy Newborn Screening-Results from Year 1 Pilot Project

enthalten in: International journal of neonatal screening | 2023

von Niri, F. | Nicholls, J. | Baptista Wyatt, K. | +11

5

Understanding the experiences of lung volume recruitment among boys with Duchenne muscular dystrophy : A multicenter qualitative study

enthalten in: Pediatric pulmonology | 2023

von Katz, S. | Blinder, H. | Newhook, D. | +10

6

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy : Results From the Phase 2, Open-Label, 4-Year Extension Study

enthalten in: Journal of neuromuscular diseases | 2023

von Clemens, P. | Rao, V. | Connolly, A. | +8

7

Corneal nerve and nerve conduction abnormalities in children with type 1 diabetes

enthalten in: Pediatric diabetes | 2022

von Pacaud, D. | Romanchuk, K. | Virtanen, H. | +6

8

Machine learning classification of multiple sclerosis in children using optical coherence tomography

enthalten in: Multiple sclerosis (Houndmills, Basingstoke, England) | 2022

von Ciftci Kavaklioglu, B. | Erdman, L. | Goldenberg, A. | +15

9

Dual-energy X-ray absorptiometry measures of lean body mass as a biomarker for progression in boys with Duchenne muscular dystrophy

enthalten in: Scientific reports | 2022

von Sherlock, S. | Palmer, J. | Wagner, K. | +8

10

Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy : A Randomized Clinical Trial

enthalten in: JAMA neurology | 2022

von Guglieri, M. | Clemens, P. | Perlman, S. | +43

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