Suchergebnisse - "Goemans, Nathalie"

PubPharm (196)

1

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS) : a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

enthalten in: The Lancet. Neurology | 2024

von Mercuri, E. | Vilchez, J. | Boespflug-Tanguy, O. | +25

ErratumIn: Lancet Neurol. 2024 Apr 18;:. - PMID 38643778

2

Reference curves of motor function outcomes in young steroid-naïve males with Duchenne muscular dystrophy

enthalten in: Developmental medicine and child neurology | 2024

von Hoskens, J. | Schiava, M. | Goemans, N. | +7

3

Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy : A Randomized Controlled Trial

enthalten in: Neurology | 2024

von Dang, U. | Damsker, J. | Guglieri, M. | +41

4

Reference curves of motor function outcomes in young steroid‐naïve males with Duchenne muscular dystrophy

enthalten in: Developmental Medicine & Child Neurology | 2024

von Hoskens, J. | Schiava, M. | Goemans, N. | +7

5

Comparison of two corticosteroid regimens on brain volumetrics in patients with Duchenne muscular dystrophy

enthalten in: Annals of clinical and translational neurology | 2023

von Geuens, S. | Van Dessel, J. | Govaarts, R. | +8

6

269th ENMC international workshop : 10 years of clinical trials in Duchenne muscular dystrophy - What have we learned? 9-11 December 2022, Hoofddorp, The Netherlands

enthalten in: Neuromuscular disorders : NMD | 2023

von Naarding, K. | Stimpson, G. | Ward, S. | +5

7

The impact of clinical trial participation on quality of life and psychosocial well-being in children with Duchenne muscular dystrophy and their parents

enthalten in: Neuromuscular disorders : NMD | 2023

von Geuens, S. | Willen, J. | Antonis, C. | +6

8

Correction to : Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study

enthalten in: Neurology and therapy | 2023

von Chiriboga, C. | Bruno, C. | Duong, T. | +114

ErratumFor: Neurol Ther. 2023 Apr;12(2):543-557. - PMID 36780114

9

Psychopharmaceutical treatment for neurobehavioral problems in Duchenne muscular dystrophy : a descriptive study using real-world data

enthalten in: Neuromuscular disorders : NMD | 2023

von Weerkamp, P. | Geuens, S. | Collin, P. | +5

10

Risdiplam in types 2 and 3 spinal muscular atrophy : A randomised, placebo-controlled, dose-finding trial followed by 24 months of treatment

enthalten in: European journal of neurology | 2023

von Mercuri, E. | Baranello, G. | Boespflug-Tanguy, O. | +19

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