Suchergebnisse - "Furlong, Pat"

PubPharm (46)

1

Moving Beyond the 2018 Minimum International Care Considerations for Osteoporosis Management in Duchenne Muscular Dystrophy (DMD) : Meeting Report from the 3rd International Muscle-Bone Interactions Meeting 7th and 14th November 2022

enthalten in: Journal of neuromuscular diseases | 2024

von Phung, K. | Crabtree, N. | Connolly, A. | +17

2

Draft Guidance for Industry Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and Related Dystrophinopathies - Developing Potential Treatments for the Entire Spectrum of Disease

enthalten in: Journal of neuromuscular diseases | 2024

von McDonald, C. | Camino, E. | Escandon, R. | +8

3

Healthcare Stakeholder Perspectives on a Value Assessment Approach for Duchenne Muscular Dystrophy Therapies

enthalten in: bioRxiv.org | 2023

von Fischer, R. | Furlong, P. | Kennedy, A. | +11

4

Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2) : a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial

enthalten in: Lancet (London, England) | 2022

von McDonald, C. | Marbán, E. | Hendrix, S. | +54

CommentIn: Lancet. 2022 Mar 12;399(10329):1024-1025. - PMID 35279246

5

Improving Access and Quality of Health Care in the United States : Shared Goals Among Patient Advocates

enthalten in: The patient | 2021

von Oehrlein, E. | Harris, J. | Balch, A. | +4

6

Development of a Clinical Global Impression of Change (CGI-C) and a Caregiver Global Impression of Change (CaGI-C) measure for ambulant individuals with Duchenne muscular dystrophy

enthalten in: Health and quality of life outcomes | 2021

von Staunton, H. | Trennery, C. | Arbuckle, R. | +5

7

Development of a Clinical Global Impression of Change (CGI-C) and a Caregiver Global Impression of Change (CaGI-C) measure for ambulant individuals with Duchenne muscular dystrophy

enthalten in: Health and quality of life outcomes | 2021

von Staunton, H. | Trennery, C. | Arbuckle, R. | +5

8

Gene therapy companies have an ethical obligation to develop expanded access policies

enthalten in: Molecular therapy : the journal of the American Society of Gene Therapy | 2021

von Kearns, L. | Chapman, C. | Moch, K. | +5

CommentIn: Mol Ther. 2021 Jun 2;29(6):1936. - PMID 33964226

9

Improving Access and Quality of Health Care in the United States: Shared Goals Among Patient Advocates

enthalten in: The Patient | 2020

von Oehrlein, E. | Harris, J. | Balch, A. | +4

10

Improving Access and Quality of Health Care in the United States: Shared Goals Among Patient Advocates

enthalten in: The Patient | 2020

von Oehrlein, E. | Harris, J. | Balch, A. | +4

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