Suchergebnisse - "Flotte, Terence R"

PubPharm (407)

1

Intrathecal gene therapy for neurologic disease in humans

enthalten in: Molecular therapy : the journal of the American Society of Gene Therapy | 2024

von Flotte, T.

2

In memoriam : Kenneth I. Berns, MD, PhD (1938-2024)

enthalten in: Molecular therapy : the journal of the American Society of Gene Therapy | 2024

von Byrne, B. | Flotte, T. | Herzog, R. | +1

3

Kenneth I. Berns, MD, PhD [1938-2024

enthalten in: Human gene therapy | 2024

von Byrne, B. | Flotte, T. | Herzog, R. | +1

4

Biodistribution and safety of a single rAAV3B-AAT vector for silencing and replacement of alpha-1 antitrypsin in Cynomolgus macaques

enthalten in: Molecular therapy. Methods & clinical development | 2024

von Blackwood, M. | Gruntman, A. | Tang, Q. | +9

5

Delivery of Adeno-Associated Virus Vectors to the Central Nervous System for Correction of Single Gene Disorders

enthalten in: International journal of molecular sciences | 2024

von Daci, R. | Flotte, T.

6

Approaches to Therapeutic Gene Editing in Alpha-1 Antitrypsin Deficiency

enthalten in: Methods in molecular biology (Clifton, N.J.) | 2024

von Gruntman, A. | Xue, W. | Flotte, T.

7

Alpha-1 Antitrypsin Deficiency

enthalten in: Methods in molecular biology (Clifton, N.J.) | 2024

von Gruntman, A. | Xue, W. | Flotte, T.

8

Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy. Reply

enthalten in: The New England journal of medicine | 2023

von Lek, A. | Keeler, A. | Flotte, T.

CommentOn: N Engl J Med. 2023 Sep 28;389(13):1203-1210. - PMID 37754285

9

Lived Experience with Gene Therapy

enthalten in: Human gene therapy | 2023

von Flotte, T.

10

Annual Editor's Letter

enthalten in: Human gene therapy | 2023

von Flotte, T.

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