Suchergebnisse - "Catalano, Fabio"

PubPharm (2)

1

Lentiviral Gene Therapy for Mucopolysaccharidosis II with Tagged Iduronate 2-Sulfatase Prevents Life-Threatening Pathology in Peripheral Tissues But Fails to Correct Cartilage

enthalten in: Human gene therapy | 2024

von Catalano, F. | Vlaar, E. | Dammou, Z. | +11

2

Tagged IDS causes efficient and engraftment-independent prevention of brain pathology during lentiviral gene therapy for Mucopolysaccharidosis type II

enthalten in: Molecular therapy. Methods & clinical development | 2023

von Catalano, F. | Vlaar, E. | Katsavelis, D. | +12

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