Thema
Journal Article
72
Research Support, Non-U.S. Gov't
29
Randomized Controlled Trial
21
Duchenne muscular dystrophy
17
Multicenter Study
17
Research Support, N.I.H., Extramural
11
Review
11
Dystrophin
10
Clinical Trial, Phase III
9
Prednisone
8
VB0R961HZT
8
spinal muscular atrophy
8
Biomarkers
7
SMN2 protein, human
7
Survival of Motor Neuron 2 Protein
7
Clinical Trial, Phase II
6
Comparative Study
5
Pregnenediones
5
deflazacort
5
Anti-Inflammatory Agents
4
Case Reports
4
Gene therapy
4
KR5YZ6AE4B
4
Oligonucleotides
4
Prednisolone
4
nusinersen
4
5Z9SP3X666
3
9PHQ9Y1OLM
3
Academic-led clinical trial
3
Clinical trial
3
Clinical trial regulations
3
DMD protein, human
3
Rare disease
3
SMN1 protein, human
3
Survival of Motor Neuron 1 Protein
3
Zolgensma
3
safety
3
33X04XA5AT
2
4-Aminopyridine
2
AIW6036FAS
2
Adrenal Cortex Hormones
2
Amifampridine
2
Amifampridine phosphate
2
Ammonia
2
BH3B64OKL9
2
Biological Products
2
Carbonic Anhydrase Inhibitors
2
Codon, Nonsense
2
FSHD
2
LEMS
2
mehr ...