Thema
Journal Article
12
Research Support, Non-U.S. Gov't
5
Iron-Binding Proteins
2
Research Support, N.I.H., Extramural
2
Review
2
ataxia
2
clinical trial
2
frataxin
2
9007-49-2
1
Actimmune
1
DNA
1
DNA Methylation
1
DNA Repeat Expansion
1
DNA methylation
1
EPI743
1
FXN gene
1
Frataxin
1
Friedreich ataxia
1
Friedreich ataxia (FRDA)
1
Friedreich's ataxia
1
Letter
1
Movement Disorders
1
NF-E2-Related Factor 2
1
NRF2
1
OXCT1
1
Omaveloxolone
1
Protein Isoforms
1
SIRT6
1
antioxidant
1
biomarkers
1
cerebellum
1
clinical care guideline
1
disease burden
1
endpoints
1
epialleles
1
epigenetic
1
epigenetics
1
gene therapy
1
glutamatergic and GABAergic synapses
1
histone deacetylase inhibitors (HDACi)
1
ketone body
1
mRNA profiling
1
mitochondria dynamics
1
mitochondrion
1
modifier
1
multisystem
1
multivariable regression
1
outcome measures
1
phase II trials
1
somatic heterogeneity
1
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