Thema
Journal Article
136
Research Support, Non-U.S. Gov't
71
Research Support, N.I.H., Extramural
36
Multicenter Study
20
Review
16
Randomized Controlled Trial
14
Spinal muscular atrophy
13
Duchenne muscular dystrophy
12
nusinersen
12
RNA-Binding Proteins
10
Risdiplam
10
spinal muscular atrophy
10
5Z9SP3X666
9
Oligonucleotides
9
RNA
9
Clinical Trial, Phase III
8
Muscular dystrophy
8
63231-63-0
7
Dystrophin
7
Myotonic dystrophy
7
Atchafalaya River
6
Fourleague Bay
6
Nerve Tissue Proteins
6
Pyrimidines
6
76RS4S2ET1
5
Azo Compounds
5
DMPK protein, human
5
EC 2.7.11.1
5
Myotonin-Protein Kinase
5
Research Support, U.S. Gov't, P.H.S.
5
onasemnogene abeparvovec
5
quality of life
5
Baton Rouge
4
Biological Products
4
Biomarkers
4
Case Reports
4
Clinical Trial, Phase II
4
Glucocorticoids
4
MDHI
4
MRI
4
Myostatin
4
Oligonucleotides, Antisense
4
PFDD
4
Protein Serine-Threonine Kinases
4
Published Erratum
4
RNA, Messenger
4
Research Support, U.S. Gov't, Non-P.H.S.
4
SMA
4
Wetland restoration
4
biomarker
4
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