Thema
Journal Article
98
Research Support, Non-U.S. Gov't
27
Research Support, U.S. Gov't, P.H.S.
27
Duchenne muscular dystrophy
26
Research Support, N.I.H., Extramural
20
Review
15
Multicenter Study
13
Randomized Controlled Trial
11
Prednisone
9
VB0R961HZT
9
Case Reports
8
Duchene muscular dystrophy
8
Duchenne Muscular Dystrophy
8
Adrenal Cortex Hormones
7
Immunosuppressive Agents
7
Comparative Study
6
Glucocorticoids
6
5Z9SP3X666
5
Becker muscular dystrophy
5
Dystrophin
5
Oligonucleotides
5
Pregnenediones
5
newborn screening
5
nusinersen
5
Becker Muscular Dystrophy
4
Caregivers
4
Clinical trial
4
Duchenne
4
KR5YZ6AE4B
4
Muscular dystrophies
4
Muscular dystrophy
4
Neurology
4
Neuromuscular disorders
4
Newborn screening
4
Quality of life
4
Rare disease
4
Spinal muscular atrophy
4
deflazacort
4
neurology
4
neuromuscular disorders
4
treatment
4
Academic-led clinical trial
3
Carbonic Anhydrase Inhibitors
3
Clinical trial regulations
3
CoQ10
3
Comment
3
DMD protein, human
3
Diagnosis
3
Dichlorphenamide
3
Diseases
3
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