TREATMENT OF NEUROLOGICAL DISEASES

Provided are methods and composition for treating certain neurodegenerative diseases, such as RGC loss-related degenerative disease and Parkinson's Disease, using in vivo conversion of glial cells to neurons by PTB and optionally nPTB knock down via CRISPR/Cas delivered by AAV vectors..

Medienart:

Patent

Erscheinungsjahr:

2024

Erschienen:

2024

Enthalten in:

Europäisches Patentamt - (2024) vom: 15. Feb. Zur Gesamtaufnahme - year:2024

Sprache:

Englisch

Beteiligte Personen:

ZHOU HAIBO [VerfasserIn]
HU XINDE [VerfasserIn]
SU JINLIN [VerfasserIn]

Links:

Volltext [kostenfrei]

Themen:

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Anmerkungen:

Source: www.epo.org (no modifications made), First posted: 2024-02-15, Last update posted on www.tib.eu: 2024-03-06, Last updated: 2024-03-08

Patentnummer:

US2024050589

Förderinstitution / Projekttitel:

PPN (Katalog-ID):

EPA019279388