METHODS OF TREATING ERYTHROPOIETIC PROTOPORPHYRIA, X-LINKED PROTOPORPHYRIA, OR CONGENITAL ERYTHROPOIETIC PORPHYRIA WITH GLYCINE TRANSPORT INHIBITORS

The present embodiments are directed to methods of using glycine transporter inhibitors, such as GlyT1 inhibitors, or pharmaceutically acceptable salts, solvates or prodrugs thereof, or pharmaceutical compositions thereof, for preventing or treating erythropoietic protoporphyria (EPP), X-linked protoporphyria (XLPP), and/or congenital erythropoietic porphyria (CEP), and related syndromes thereof..

Medienart:

Patent

Erscheinungsjahr:

2024

Erschienen:

2024

Enthalten in:

Europäisches Patentamt - (2024) vom: 03. Apr. Zur Gesamtaufnahme - year:2024

Sprache:

Englisch

Beteiligte Personen:

MACDONALD BRIAN RICHARD [VerfasserIn]
BECONI MARIA GABRIELA [VerfasserIn]
HONG VU [VerfasserIn]

Links:

Volltext [kostenfrei]

Themen:

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Anmerkungen:

Source: www.epo.org (no modifications made), First posted: 2024-04-03, Last update posted on www.tib.eu: 2024-04-16, Last updated: 2024-04-19

Patentnummer:

EP4087570

Förderinstitution / Projekttitel:

PPN (Katalog-ID):

EPA000109169