Suchergebnisse - "Caizergues, Didier"

PubPharm (6)

1

A decade of optimizing drug development for rare neuromuscular disorders through TACT

enthalten in: Nature reviews. Drug discovery | 2020

von Wagner, K. | De Luca, A. | Caizergues, D. | +13

2

Report on the workshop : Meaningful outcome measures for Duchenne muscular dystrophy, London, UK, 30-31 January 2017

enthalten in: Neuromuscular disorders : NMD | 2018

von Straub, V. | Mercuri, E. | DMD outcome measure study group | +28

3

The TREAT-NMD advisory committee for therapeutics (TACT) : an innovative de-risking model to foster orphan drug development

enthalten in: Orphanet journal of rare diseases | 2015

von Heslop, E. | Csimma, C. | Straub, V. | +85

4

The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development

enthalten in: Orphanet journal of rare diseases | 2015

von Heslop, E. | Csimma, C. | Straub, V. | +12

5

A phase I trial of adeno-associated virus serotype 1-{gamma}-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C

enthalten in: Brain | 2012

von Herson, S. | Hentati, F. | Rigolet, A. | +25

6

A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C

enthalten in: Brain : a journal of neurology | 2012

von Herson, S. | Hentati, F. | Rigolet, A. | +25

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